Duchenne UK

Duchenne Muscular Dystrophy (DMD) is a devastating muscle-wasting disease. It is the most common and severe form of Muscular Dystrophy. Diagnosed in childhood, it mainly affects boys. There is currently no cure. Started by families affected by the disease, Duchenne UK has one clear aim – to end Duchenne.

Duchenne UK connects leading researchers with industry, the NHS and patients to challenge every stage of drug development, from research to clinical trials to drug approval. They connect families with each other to create a network of mutual support and to pool resources, knowledge and experience.

Duchenne UK have created a new infrastructure to deliver potentially life-saving clinical trials through the DMD Hub. They also fund the doctors, nurses, physiotherapists and trial coordinators needed to run these trials. They have uncovered treatments and enabled them to be delivered to patients. They have enabled quick access to new treatments through their campaigning and Project HERCULES which has established an innovative way to connect leading DMD drug developers.

Duchenne UK’s heart and soul, and reason for carrying on, are the boys and men, and rare girls, living with DMD.

Together, we will end Duchenne.